The strategy and prospect of gene therapy in neurogenetic diseases
10.3760/cma.j.issn.1006-7876.2018.11.001
- VernacularTitle:神经遗传病的基因治疗策略与前景
- Author:
Ning WANG
1
;
Miao ZHAO
;
Wanjin CHEN
Author Information
1. 福建医科大学附属第一医院神经内科
- Keywords:
Neurogenetic diseases;
Gene therapy;
Strategy;
Prospect
- From:
Chinese Journal of Neurology
2018;51(11):857-862
- CountryChina
- Language:Chinese
-
Abstract:
Most of the neurogenetic disorders could not be cured until now. With the development of molecular biological techniques, gene therapies show brilliant application prospects in neurogenetic disorders, which contain gene supplementation, exon skipping, splicing enhancement, dynamic mutation correction and toxic expression product elimination, and so on.
