Advance in therapy for Duchenne/Becker muscular dystrophy.
- Author:
Tian-Tian XU
1
;
Dan LAN
Author Information
1. Department of Pediatrics, First Affiliated Hospital of Guangxi Medical University, Nanning 530021, China. land6785@163.com.
- Publication Type:Journal Article
- MeSH:
Genetic Therapy;
Glucocorticoids;
therapeutic use;
Humans;
Muscular Dystrophy, Duchenne;
therapy;
Stem Cell Transplantation
- From:
Chinese Journal of Contemporary Pediatrics
2015;17(3):294-298
- CountryChina
- Language:Chinese
-
Abstract:
Duchenne/Becker muscular dystrophy (DMD/BMD) is the most common X-linked recessive inherited neuromuscular disease, characterized by progressive muscle weakness. Mutations in the dystrophin gene are responsible for this disease. Treatment for this disease has always been a topic of interest. With the development of diagnosis and treatment technology of molecular biology, promising therapies have been developed. This review article summarizes the advance in traditional therapy, cell transplantation and gene therapy for this disease.
