Current views on rare diseases research and orphan drugs development.
- Author:
Jingwen JIANG
1
;
Jing LI
;
Wenjun LIU
Author Information
1. School of Life Sciences, University of Science and Technology of China, Hefei 230027, China
- Publication Type:Journal Article
- MeSH:
China;
Humans;
Orphan Drug Production;
Rare Diseases;
genetics;
therapy
- From:
Chinese Journal of Biotechnology
2011;27(5):724-729
- CountryChina
- Language:Chinese
-
Abstract:
Interest in rare diseases research and orphan drugs development has been increased distinctly in recent years. The number of affected people with rare diseases is considerable around the world and the formulation of national and international incentive policies to accelerate orphan drugs development, aiming at offering facilities and necessary conditions for patient access to treatment, gains favorable results. In particular, more measures should be taken to catalyze further progress due to behindhand level in this field in China. Additionally, therapeutic methods of rare diseases were also discussed.