Research status of hemophilia treatment
10.13699/j.cnki.1001-6821.2018.19.023
- VernacularTitle:血友病治疗的研究现状
- Author:
Shuang-Min JI
1
;
Xi-Wei JI
;
Ai-Ping YU
;
Chen-Yan GAO
Author Information
1. 国家食品药品监督管理总局 药品审评中心
- Keywords:
hemophilia;
coagulation factor;
gene therapy;
progress
- From:
The Chinese Journal of Clinical Pharmacology
2018;34(19):2359-2361,2365
- CountryChina
- Language:Chinese
-
Abstract:
Hemophilia is genetic bleeding disorder , and the replacement therapy by the infusion coagulation factors provides an available effective for hemophilia.With the drug development at home and abroad , signifi-cant progress has been achieved in the field of hemophilia treatment in recent years, including the design of long -acting clotting factor prepara-tions, gene therapy, and novel agents.This study provides a brief over-view of current therapies for hemophilia and reviews the latest develop-ments in its treatment.
